New Downloadable Resources
Video
MDA Industry Forum 2021: AAV Gene Therapy - Considerations for a Viral Vector Platform
Video
MDA Industry Forum 2021: AAV Gene Therapy - Production and Practicalities
Video
MDA Industry Forum 2021: Clinical Review of AAV Gene Therapy - Lessons for the Future
Video
MDA Industry Forum 2021: Gene Therapy - Evolving the Treatment Landscape
Downloadable Resources
Video
Institutional Readiness
An animated video demonstrating biosafety handling guidance
Slides
Biosafety Considerations
Establishing the biological risk and appropriate containment for
gene therapy agents
Slides
Gene Therapy Approvals
Summary of approved gene therapy agents
Video
The Process of Gene Replacement Therapy
A video showing how gene replacement therapy works
Video
Recorded Webinar: Practical Considerations for the Use Of In Vivo AAV-Based Gene Therapies
An overview of the biological risks and containment practices for use of AAV-based gene therapies presented by Dr. Chris Jenkins
Slides
GTnetwork Delivery of Gene Therapy
A summary of delivery systems and methods for gene therapy
Slides
GTnetwork Biosafety Handling for Gene Replacement Therapy
Overview of gene therapy and biosafety handling considerations
Slides
GTnetwork Gene Therapy Clinical Trials
Disease targets and approved clinical trials by year from 1989–2018
Slides
GTnetwork Genetic Diseases & Gene Therapy Approaches
Review of targeted disease types and approaches for monogenic diseases
Slides
Webinar Slides: Practical Considerations for the Use of In Vivo AAV-Based Gene Therapies
An overview of the biological risks and containment practices for use of AAV-based gene therapies presented by Dr. Chris Jenkins [webinar slides]
Slides
GTnetwork Gene Replacement Therapy
Overview of gene replacement therapy as a treatment strategy
Slides
GTnetwork Gene Manipulation Strategies
Manipulation strategies utilized for gene therapy
Slides
GTnetwork Gene Therapy Milestones
Timeline of major milestones
Webinar Q&A: Practical Considerations for the Use Of In Vivo AAV-Based Gene Therapies
Participant Q&As with Dr. Chris Jenkins from the "Practical Considerations for the Use Of In Vivo AAV-Based Gene Therapies" webinar
GTnetwork AAV Biosafety Summary
Summary of biosafety considerations related to AAV-based gene therapies
