The mission of the GTnetwork is to build knowledge of the evolving gene therapy landscape among healthcare professionals by providing engaging, evidence-based educational content while fostering peer-to-peer interaction.

Objectives: Educational Content

The GTnetwork educational content includes a comprehensive curriculum covering a range of topics from the basic principles of gene therapy to the clinical evidence behind the design, delivery, and use of gene therapy. 

The gene therapy landscape is constantly evolving, therefore new content for the GTnetwork will be developed and released over time.

The GTnetwork educational content will:
  • Review potential disease targets for gene therapy

  • Provide insight into the clinically relevant aspects of the design and manufacturing of gene therapies

  • Explain the different therapeutic gene alteration strategies and their clinical uses

  • Discuss ongoing practical considerations for the use of gene therapy in the clinic

Meet The Steering Committee

All GTnetwork content is overseen and reviewed by a multidisciplinary, internationally renowned steering committee of experts. This group provides leadership and insight into the platform’s content and features, as well as answering questions from the community and discussing “hot topics”.


Diana Bharucha-Goebel

Director of the Muscular Dystrophy Association Care Center and Assistant Professor in the Division of Neurology
READ DR. bharucha-goebels bio

Arthur Burghes

Professor at Wexner Medical Center College of Medicine in the Department of Biological Chemistry and Pharmacology

Jahannaz Dastgir

Medical Director of the Pediatric Neuromuscular Medicine Program at Goryeb Children’s Hospital
READ DR. Dastgirs bio

Chris Jenkins

Principal Partner and Chief Gene Therapy Biosafety Officer at Clinical Biosafety Services
READ DR. Jenkins bio

Alex MacKenzie

Principal Investigator at the
Children’s Hospital of Eastern Ontario

READ DR. MacKenzies bio

Loren del Mar Peña

Associate Professor of Pediatrics
at the University of Cincinnati, Ohio
READ DR. Peñas bio

John Petrich

Director Investigational Drug Services at the Cleveland Clinic
READ DR. Petrichs bio