Welcome to the leading edge of gene therapy education

The Gene Therapy Network provides the latest, expert-led, educational and practical gene therapy content, based on the needs of healthcare professionals around the world and aligned with professional bodies

MODULE 1

Overview of Gene Therapy

An overview of gene therapy and some of the key concepts in this field

MODULE 2

Monogenic and Complex Diseases

An overview of genetic abnormalities and current treatment strategies for monogenic diseases

MODULE 3

Safety of Gene Therapy

A review of the two types of immune responses in the context of two of the most widely studied viral vectors

MODULE 4

Practical Considerations

An overview of the biological risks and containment practices for use of AAV-based gene therapies

MODULE 5

Gene Replacement

One important approach to gene therapy is gene replacement. This video further explores this important concept.

MODULE 6

Current Therapeutics & Research

A review of the gene therapy development landscape and exploration of marketed agents

NEWS

STEERING COMMITTEE

Meet our multidisciplinary, internationally renowned steering committee of experts:

Chris Jenkins, PhD, MPH

Chairperson
Principal Partner and Chief Gene Therapy Biosafety Officer at Clinical Biosafety Services

Diana Bharucha-Goebel, MD

Director of the Muscular Dystrophy Association Care Center and Assistant Professor in the Division of Neurology

Arthur Burghes, PhD

Professor at Wexner Medical Center College of Medicine in the Department of Biological Chemistry and Pharmacology

James Dowling, MD, PhD, FANA

Professor of Pediatrics and Molecular Genetics at the University of Toronto

Uta Griesenbach, DIPL-BIOL, PhD

Professor in Molecular Medicine at the National Heart and Lung Institute at Imperial College London

Kristi Jones, PhD

Clinical Associate Professor of Pediatrics, Child Health and Genetic Medicine at The University of Sydney, and Co-Head of the Department of Clinical Genetics at The Children’s Hospital at Westmead

John Petrich, MS, RPh

Director Investigational Drug Services at the Cleveland Clinic